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Small-molecule activation of lysosomal TRP channels ameliorates Duchenne muscular dystrophy in mouse models
- Yu, Lu
;
- Zhang, Xiaoli
;
- Yang, Yexin
;
- Li, Dan
;
- Tang, Kaiyuan
;
- Zhao, Zifan
;
- He, Wanwan
;
- Wang, Ce
;
- Sahoo, Nirakar
;
- Converso-Baran, Kimber
;
- Davis, Carol S.
;
- Brooks, Susan V.
;
- Bigot, Anne
;
- Calvo, Raul
;
- Martinez, Natalia J.
;
- Southall, Noel
;
- Hu, Xin
;
- Marugan, Juan
;
- Ferrer, Marc
;
- Xu, Haoxing
- Publication:
-
Science Advances
- Pub Date:
- February 2020
- DOI:
-
10.1126/sciadv.aaz2736
- Bibcode:
-
2020SciA....6.2736Y
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