Safety, Tolerability, and Pharmacokinetics of SMT C1100, a 2-Arylbenzoxazole Utrophin Modulator, following Single- and Multiple-Dose Administration to Pediatric Patients with Duchenne Muscular Dystrophy
Abstract
- Publication:
-
PLoS ONE
- Pub Date:
- April 2016
- DOI:
- 10.1371/journal.pone.0152840
- Bibcode:
- 2016PLoSO..1152840R